WASHINGTON (AP) — Federal health regulators have questions about the benefits of an experimental combination drug for cystic fibrosis, including whether the addition of a second drug ingredient adds ...

A Cystic Fibrosis drug targeting the basic defect that causes the condition has been shown to be safe and effective in newborns aged four weeks and above, new research involving RCSI University of ...

Cystic fibrosis miracle drug Trikafta, helps 90% of people, the other 10% are still waiting for their aid. The small box full of promises arrived at Jessica Anderson’s home on her 31st birthday. A ...

The first drug that treats the root cause of cystic fibrosis won approval Tuesday, offering a life-changing treatment for a handful of patients with the deadly illness and broader hope for thousands ...

(RTTNews) - Vertex Pharmaceuticals Inc. (VRTX) Friday announced that the U.S. Food and Drug Administration (FDA) has approved Alyftrek for treatment of cystic fibrosis. Alyftrek is a once-daily ...

Colorado’s new prescription drug review board decided in a first-in-the-nation vote that a medication costing more than $200,000 a year doesn’t qualify as “unaffordable,” based on the drug’s benefits ...

CHANNAHON, Ill. (WLS) -- Brandon Wolfe enjoys spending quality time with his family. Playing with his young sons wasn't always easy, but he has a lot more energy to play after testing a new drug to ...

Vertex Pharmaceuticals, known for its line of cystic fibrosis drugs, has entered the gene editing space with a new $105 million deal with CRISPR Therapeutics. Cystic fibrosis has become the poster ...

People with cystic fibrosis who begin the triple-drug therapy elexacaftor tezacaftor ivacaftor are able to safely scale down many of their routine lung therapies while preserving good health for years ...

Boston-based Vertex Pharmaceuticals is in a dispute with Canadian officials over access to its cystic fibrosis drugs, STAT reported. The dispute focuses on three of Vertex’s drugs, Kalydeco, Orkambi ...

A drug commonly used to treat cystic fibrosis improved outcomes for patients with severe COVID-19 pneumonia and could be used to treat other respiratory infections, according to clinical trial results ...

Emily Pink and Stuart Priscott both suffer from cystic fibrosis and take Kaftrio to manage their symptoms - Jay Williams / John Lawrence Emily Pink, 21, has cystic fibrosis, a rare genetic disorder ...