A well-connected family’s fight to access a potential treatment for their son highlights the barriers most rare disease patients struggle to overcome.

1. ZANVASTRO (zilganersen) approved by the FDA as the first and only disease modifying treatment for Alexander disease (AxD) ...

After nearly a decade, Ridley Scott is returning to the Alien franchise with a contemporary take. The Academy Award honoree recently revealed that he’s “rewriting the next Alien film,” which will ...

Ridley Scott does not seem to be thinking of retiring anytime soon. Not only does the director, 88, have Jacob Elordi starrer “The Dog Stars” opening Friday, he’s planning to put his own stamp on ...

Hip bursitis diagnosis and relief: understanding trochanteric pain syndrome treatment options Jamie Lee Curtis breaks down remembering Emmy-winning co-star Kash Patel’s bizarre hearing went from ...

In evaluation of photographs from before and after the intervention, improvements in HFS-related skin symptoms were observed in 31 patients (58.5%). All evaluated patients were also able to complete ...

Data presented at the EHA Congress 2026 showed dynamic results for patients with multiple myeloma assigned to the BCMA-sparing bispecific antibody talquetamab and mezigdomide plus carfilzomib and ...

Deaf children can now hear thanks to a new treatment that repairs a defective gene. Researchers associated with the biotech company Regeneron Pharmaceuticals unveiled the successful gene therapy last ...

I was diagnosed with IBS and feel like that basically means no one knows what’s going on. I’ve seen people recommend things like abdominal massages online. Would that help? The biggest misconception I ...

Short bowel syndrome (SBS) occurs when a large portion of the small intestine is missing, damaged, or affected by disease, making it difficult to absorb nutrients and fluids. Treatment varies by stage ...

We recently got our first look at a UFO in Steven Spielberg‘s upcoming sci-fi film Disclosure Day, and now we’re getting our first look at an alien. A new trailer has been released, offering the first ...

Please provide your email address to receive an email when new articles are posted on . Endovascular therapy (EVT) for post-thrombotic syndrome improved symptom severity and patient-reported quality ...