Oska-Gray Valentine-Colquhoun, 20 months old, spent his first days in the NICU after being born in distress. He had to have ...

A new Finnish study shows that adults who remain physically active throughout adulthood have a markedly lower prevalence of metabolic syndrome at age 61 than those whose leisure-time physical activity ...

As it kicks off a pivotal phase 3 trial of its investigational treatment for Angelman syndrome (AS), Ionis Pharmaceuticals is laying the groundwork for a potential launch. After spending the last ...

Ionis Pharmaceuticals, which is developing a treatment for the rare neurological disease of Angelman syndrome (AS), turned to Lifetime Television’s “Behind the Mystery” series to increase public ...

LOS ANGELES (KABC) -- Having a broken heart can mean more than an emotional wound. Broken heart syndrome is a condition where some of your heart muscle weakens rapidly and typically happens after ...

MIDDLETON, Mass., Nov. 6, 2025 /PRNewswire/ -- MavriX Bio, a clinical-stage biotechnology company focused on the development of transformative genetic therapies for Angelman syndrome (AS), today ...

Take advantage of TipRanks Premium at 50% off! Unlock powerful investing tools, advanced data, and expert analyst insights to help you invest with confidence. Ultragenyx Pharmaceutical ( (RARE)) just ...

On Tuesday, the U.S. Food and Drug Administration (FDA) granted Breakthrough Therapy designation to Ionis Pharmaceuticals Inc.’s (NASDAQ:IONS) ION582 for Angelman syndrome (AS), a rare neurological ...

CARLSBAD, Calif.--(BUSINESS WIRE)--Ionis Pharmaceuticals, Inc. (Nasdaq: IONS) today announced that the U.S. Food and Drug Administration (FDA) has granted Breakthrough Therapy designation to ION582 ...

CHESHIRE, Conn. (WTNH) — The General Motors charity car show was held on Sunday in Cheshire, benefitting families with children diagnosed with Angelman Syndrome. Quinnipiac students create customized ...